ey0019.5-2 | Novel treatments for rare skeletal disorders | ESPEYB19
A Infante
, B Gener
, M Vazquez
, N Olivares
, A Arrieta
, G Grau
, I Llano
, L Madero
, AM Bueno
, B Sagastizabal
, D Gerovska
, MJ Arauzo-Bravo
, I Astigarraga
, CI Rodriguez
Clin Transl Med. 2021 Jan;11(1):e265. Abstract: https://pubmed-ncbi-nlm-nih-gov.proxy.kib.ki.se/33463067/In brief: In order to explore safety, efficacy, and feasibility of repeated infusions of mesenchymal stem cells (MSCs) as a treatment for OI, two pediatric OI patients were treated with repeated infusions of HLA-matched MSCs. The patients tolerated the treatment well and ...